Therapeutic gene editing of ELANE for severe congenital neutropenia
Daniel Bauer, MD, PhD (Boston Children’s Hospital)
Selectin inhibitors for prevention of cancer-associated venous thromboembolism
Elliot Chaikof, MD, PhD (Beth Israel Deaconess Medical Center)
A novel therapy to achieve insulin-independent glycemic control in type 1 diabetes
Christiane Ferran, MD, PhD (Beth Israel Deaconess Medical Center)
A first-in-class therapeutic antibody for treatment of asthma
Steven Greenberg, MD (Brigham and Women’s Hospital)
Antisense oligonucleotide-based progranulin augmentation therapy in neurodegenerative diseases
Peter Park, PhD (Harvard Medical School)