Identifying small-molecule therapies for telomere diseases
Suneet Agarwal, MD, PhD (HMS Associate Professor of Pediatrics at Boston Children’s Hospital)
Gene therapy for congenital deafness and blindness
David Corey, PhD (Bertarelli Professor of Translational Medical Science, Blavatnik Institute at HMS)
Protein therapy for frozen shoulder
Ara Nazarian, Dr. Sc. (HMS Professor of Orthopedic Surgery at Beth Israel Deaconess Medical Center)
Treating pediatric anemia with gene therapy
Vijay Sankaran, MD, PhD (HMS Associate Professor of Pediatrics at Boston Children’s Hospital)